Infant with rare, incurable disease is first to successfully receive personalized gene therapy treatment

Infant with rare, incurable disease is first to successfully receive personalized gene therapy treatment

News Release Thursday, May 15, 2025 NIH-supported gene-editing platform lays groundwork to rapidly develop treatments…

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Child treated with gene editing therapy for the first time by a team of Philadelphia doctors

Child treated with gene editing therapy for the first time by a team of Philadelphia doctors

A child diagnosed with a rare genetic disorder was successfully treated with a customized CRISPR gene…

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US doctors rewrite DNA of infant with severe genetic disorder in medical first | Gene editing

US doctors rewrite DNA of infant with severe genetic disorder in medical first | Gene editing

Doctors in the US have become the first to treat a baby with a customised gene-editing…

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Gene therapy experiment treats rare childhood blindness

Gene therapy experiment treats rare childhood blindness

Smitha Mundasad Health reporter Moorfields Hospital Jace, 6, was born with a rare and aggressive eye…

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